Read More

Scholar Rock’s New 36-Month Apitegromab Extension Data Reinforce Long-Term Substantial And Sustained Improvement Of Motor Function In Phase 2 TOPAZ Trial Patients With Nonambulatory Spinal Muscular Atrophy

- Improvements in patient-reported outcomes consistent with gains in motor function scores - Safety profile at 36 months consistent with previous reports with no new safety findings; more than 90 percent of nonambulatory patients remained on study

SRRK