Scholar Rock (NASDAQ:SRRK), a Phase 3, clinical-stage biopharmaceutical company focused on the treatment of serious diseases in which protein growth factors play a fundamental role, today announced an e-poster presentation by Thomas Crawford, M.D., on the design of the company’s ongoing SAPPHIRE Phase 3 clinical trial in spinal muscular atrophy (SMA) at the 17th International Congress on Neuromuscular Diseases (ICNMD 2022) in Brussels, Belgium (July 5 – 9, 2022). The abstract will be published in the peer-reviewed Journal of Neuromuscular Diseases.
“Enrollment in the ongoing pivotal Phase 3 SAPPHIRE trial, designed to further evaluate the potential of apitegromab in people with non-ambulatory Types 2 and 3 SMA, is progressing, and we are encouraged by the enthusiasm and support of the patient and provider communities,” said Nagesh Mahanthappa, Ph.D., Founding Chief Executive Officer & President of Scholar Rock. “We look forward to this upcoming opportunity at ICNMD to share details about the SAPPHIRE trial with medical colleagues from around the world who are focused on neuromuscular disorders.”
Details of the presentation are as follows:
Title: SAPPHIRE: Efficacy and Safety of Apitegromab in later-onset SMA; Phase 3 Trial in Progress (Abstract Number 105)
Presenter: Thomas Crawford, M.D., Professor of Neurology and Pediatrics; Johns Hopkins University
Session Details: Lunch & e-Poster Session II; Topic Group 04 – SMA: Treatment
Date: Thursday, July 7, 2022
Time: 1:00-2:00 p.m. CEST
Location: The live event will occur at the ICNMD 2022 Exhibit Hall, Square – Brussels’ Convention Centre.
Scholar Rock will have a Live Booth, #107 and for those attending virtually, the virtual booth will be accessible via the ICNMD Learning Toolbox.
For conference information visit ICNMD.org.
